Table 1

OPA1 mutations in OPA1-positive ADOA patients

Patient
Gene Mutation
Exon
Protein Change
Protein Domain

P2a
c.239A>G
2
Tyr80Cys
Mt targeting

c.2883A>Cb
28
Stop961Tyr
Coiled-coiled
P3
c.2522A>G
25
Tyr841Cys
C-terminal
P4
c.2780T>A
27
Leu927Stopc
Coiled-coil
P6
c.1654delT
17
Trp552fsc
Dynamin
P7
c.1929delC
20
Thr643fsc
Dynamin
P8
c.2708delTTAG
27
Val903fsc
Coiled-coil

aCompound heterozygote.

bResults in a 3 amino acid C-terminal extension.

cMutations in OPA1 result in protein truncation at the amino acid shown.

Mayorov et al. BMC Biochemistry 2008 9:22   doi:10.1186/1471-2091-9-22